GEMMABio Launches RareTx: A New Frontier in Gene Therapy for Ultra-Orphan Diseases
In a bold move to address the unmet needs of patients with ultra-rare diseases, GEMMABio, founded by gene therapy pioneer James Wilson, M.D., Ph.D., has announced the launch of a new clinical-stage spinout company, Rare Therapeutics (RareTx). This development marks a significant step forward in the pursuit of genetic medicines for some of the most underserved patient populations worldwide.